4 campaigns raising money for rare disease, $477,040 raised so far.

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DNM1$134,089of $800,00017%LaforaWe are raising money for developing an ASO for Lafora disease$1,590of $300,0001%STXBP1$352of $1,650,0000%NEK1 fALSHelp Develop a Treatment for NEK1-Associated ALS For families facing ALS, a genetic diagnosis can offer an explanation—but it also raises an urgent question: Ca$341,009of $800,00043%